Scientific Advisors

Our 23-strong team boasts deep experience in RNA biology, bioinformatics analytics, neuro-translation and development.

Dr Tom Massey

University of Cardiff

  • Neurologist specialising in HD & repeat expansion disorders
  • Clinical trials in HD
  • Active laboratory researching DDR in HD using iPSC, CRISPR and biochemistry to link clinical phenotype to mechanism
  • Exploring therapeutic options including genetic therapies

Dr Eric Marcusson

Independent Consultant

  • Providence Therapeutics: Cofounder, CSO
  • Deep Genomics: SAB
  • Regulus: Snr Director
  • Isis Pharma: Director
  • Post-doctoral studies in oligonucleotide trafficking

Dr Jim Gusella

MGH, Harvard

  • Human geneticist
  • Identification of susceptibility and modifier genes
  • Characterisation of these genes
  • Led GeM-HD consortium that ID’d DDR genes through large GWAS studies
  • Exploring therapeutic options including genetic therapies

Dr Jennifer Sims

Independent consultant

  • More than 30 years non-clinical biologic drug development experience
  • Expert preclinical Assessor, MHRA
  • Head of BioPharma Safety Assessment Group, MedImmune
  • Head of Translational Science & Safety, Novartis Biologics

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Huntington's Disease

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ALS and Alzheimer's

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